MUSCULAR DYSTROPHY THERAPIES DELHI/INDIA FOR DUMMIES

not too long ago, the antibiotic gentamicin is tested in boys with DMD, about ten% of whom have inherited a dystrophin gene using a premature cease codon that halts the synthesis with the protein N-terminal to the dystroglycan binding area. Gentamicin suppresses chain termination, permitting some whole-size dystrophin being made. This results in im